Pompe disease gene therapy

Barry J. Byrne, Darin J. Falk, Christina A. Pacak, Sushrusha Nayak, Roland W. Herzog, Melissa E. Elder, Shelley W. Collins, Thomas J. Conlon, Nathalie Clement, Brian D. Cleaver, Denise A. Cloutier, Stacy L. Porvasnik, Saleem Islam, Mai K. Elmallah, Anatole Martin, Barbara K. Smith, David D. Fuller, Lee Ann Lawson, Cathryn S. Mah