Pompe disease gene therapy

Barry J. Byrne, Darin J. Falk, Christina A. Pacak, Sushrusha Nayak, Roland W. Herzog, Melissa E. Elder, Shelley W. Collins, Thomas J. Conlon, Nathalie Clement, Brian D. Cleaver, Denise A. Cloutier, Stacy L. Porvasnik, Saleem Islam, Mai K. Elmallah, Anatole Martin, Barbara K. Smith, David D. Fuller, Lee Ann Lawson, Cathryn S. Mah

Research output: Contribution to journalArticlepeer-review

75 Citations (Scopus)


Dive into the research topics of 'Pompe disease gene therapy'. Together they form a unique fingerprint.

Medicine and Dentistry

Pharmacology, Toxicology and Pharmaceutical Science

Immunology and Microbiology